Accelerating Rare Disease Therapies: The Regulatory Revolution in Orphan Drug Development. International Journal of Research in Pharmaceutical Sciences and Technology, [S. l.], v. 9, n. 3, 2026. DOI: 10.33974/3ps0x808. Disponível em: http://rubatosisjournals.com/index.php/ijrpst/article/view/393. Acesso em: 10 aug. 2026.